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Trials & R&D · first seen 10h ago, updated 10h ago

N-of-1 therapies to address rare diseases with no commercial interest

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Despite considerable advances in diagnosis, new gene-modifying modalities and significant regulatory inducements, there remains a long tail of rare diseases that are below the threshold required for sustainable commercial investment.

Summary from BioWorld Articles.

Coverage 1 article · 1 outlet

  1. BioWorld Articles
    N-of-1 therapies to address rare diseases with no commercial interest